Maintenance: On Thursday, June 28 2018, 18:00-18:15, maintenance work on the ZORA servers is scheduled. ZORA will not be available during this period. Thank you for your patience.
Harding, C O; Blau, N (2010). Advances and challenges in phenylketonuria. Journal of Inherited Metabolic Disease, 33(6):645-648.
Rebuffat, A; Harding, C O; Ding, Z; Thöny, B (2010). Comparison of adeno-associated virus pseudotype 1, 2, and 8 vectors administered by intramuscular injection in the treatment of murine phenylketonuria. Human Gene Therapy, 21(4):463-477.
Ding, Z; Harding, C O; Rebuffat, A; Elzaouk, L; Wolff, J A; Thöny, B (2008). Correction of murine PKU following AAV-mediated intramuscular expression of a complete phenylalanine hydroxylating system. Molecular Therapy, 16(4):673-681.