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Number of items: 6.

Rivera-Barahona, Ana; Sánchez-Alcudia, Rocío; Viecelli, Hiu Man; Rüfenacht, Veronique; Pérez, Belén; Ugarte, Magdalena; Häberle, Johannes; Thöny, Beat; Desviat, Lourdes Ruiz (2015). Functional characterization of the spf/ash splicing variation in OTC deficiency of mice and man. PLoS ONE, 10(4):e0122966.

Stoller, Fabienne; Schlegel, Andrea; Viecelli, Hiu Man; Rüfenacht, Véronique; Cesarovic, Nikola; Viecelli, Claudio; Deplazes, Sereina; Bettschart-Wolfensberger, Regula; Hurter, Karin; Schmierer, Philipp A; Sidler, Xaver; Kron, Philipp; Dutkowski, Philipp; Graf, Rolf; Thöny, Beat; Häberle, Johannes (2015). Hepatocyte transfection in small pigs after weaning by hydrodynamic intraportal injection of naked DNA/minicircle vectors. Human Gene Therapy. Methods, 26(5):181-192.

Viecelli, Hiu Man; Harbottle, Richard P; Wong, Suet Ping; Schlegel, Andrea; Chuah, Marinee K; Van den Driessche, Thierry; Harding, Cary O; Thöny, Beat (2014). Treatment of phenylketonuria using minicircle-based naked-DNA gene transfer to murine liver. Hepatology, 60(3):1035-1043.

Thöny, Beat; Ding, Zhaobing; Rebuffat, Alexandre; Viecelli, Hiu Man (2014). Phenotypic reversion of fair hair upon gene therapy of the phenylketonuria mice. Human Gene Therapy, 25(7):573-574.

Gallego-Villar, Lorena; Viecelli, Hiu Man; Pérez, Belén; Harding, Cary O; Ugarte, Magdalena; Thöny, Beat; Desviat, Lourdes R (2014). A sensitive assay system to test antisense oligonucleotides for splice suppression therapy in the mouse liver. Molecular Therapy - Nucleic Acids, 3:e193.

Viecelli, Hiu Man; Thöny, Beat (2014). Challenges of experimental gene therapy for urea cycle disorders. Journal of Pediatric Biochemistry, 4(1):65-73.

This list was generated on Mon Sep 23 05:34:14 2019 CEST.